Litcius/Paper detail

Diagnostic assay to assist clinical decisions for unclassified severe combined immune deficiency

Panojot Bifsha, Jennifer W. Leiding, Sung‐Yun Pai, A. Colamartino, Nicholas Hartog, Joseph A. Church, Benjamin Oshrine, Jennifer M. Puck, M. Louise Markert, Élie Haddad

2020Blood Advances41 citationsDOIOpen Access PDF

Abstract

Key Points 3D organoid T-cell differentiation from a few hundred peripheral blood CD34+ cells was successfully achieved. 3D organoid T-cell differentiation could help physicians distinguish intrinsic from extrinsic defects underlying a clinical SCID phenotype.

Topics & Concepts

OrganoidImmune systemPhenotypeCD34ImmunologyPeripheral bloodMedicineCellular differentiationBiologyBioinformaticsStem cellNeuroscienceCell biologyGeneticsGeneImmunodeficiency and Autoimmune DisordersBlood disorders and treatmentsCytomegalovirus and herpesvirus research