Highly conserved brain vascular receptor ALPL mediates transport of engineered AAV vectors across the blood-brain barrier
Tyler C. Moyer, Brett Hoffman, Weitong Chen, Ishan Shah, Xiao‐Qin Ren, Tatiana M. Knox, Jiachen Liu, Wei Wang, Jiangyu Li, Hamza Khalid, Anupriya S. Kulkarni, Munachiso Egbuchulam, Joseph Clement, Alexis Bloedel, Matthew A. Child, Rupinderjit Kaur, Emily Rouse, Kristin Graham, Damien Maura, Zachary Thorpe, Ambreen Sayed-Zahid, Charlotte Hiu-Yan Chung, A. V. Kutchin, Amy J. Johnson, Johnny Yao, Jeffrey S. Thompson, Nilesh Pande, Mathieu Nonnenmacher
Topics & Concepts
Blood–brain barrierCell biologyBiologyReceptorNeuroscienceCentral nervous systemGeneticsAdenosine and Purinergic SignalingVirus-based gene therapy researchComplement system in diseases