Treating Bietti crystalline dystrophy in a high-fat diet-exacerbated murine model using gene therapy
Bin Qu, Shijing Wu, Guanyi Jiao, Xuan Zou, Zhikun Li, Lu Guo, Xuehan Sun, Cheng Huang, Zixi Sun, Ying Zhang, Hui Li, Qi Zhou, Ruifang Sui, Wei Li
Topics & Concepts
Genetic enhancementBiologyDystrophyGene deliveryElectroretinographyRetinalGeneRetinal degenerationBlindnessRetinaVector (molecular biology)EndocrinologyGeneticsMedicineNeuroscienceBiochemistryRecombinant DNAOptometryRetinal Development and DisordersCRISPR and Genetic EngineeringRNA regulation and disease