CFTR modulator therapy for cystic fibrosis caused by the rare c.3700A>G mutation
Puay‐Wah Phuan, Peter M. Haggie, Joseph Tan, Amber A. Rivera, Walter E. Finkbeiner, Dennis W. Nielson, Merlin Thomas, Ibrahim A. Janahi, A. S. Verkman
Topics & Concepts
Cystic fibrosisMedicineMutationCystic fibrosis transmembrane conductance regulatorInternal medicineGastroenterologyGeneticsGeneBiologyCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchAsthma and respiratory diseases