Intra-cisterna magna delivery of an AAV vector with the GLUT1 promoter in a pig recapitulates the physiological expression of SLC2A1
Sachie Nakamura, Hitoshi Osaka, Shin‐ichi Muramatsu, Naomi Takino, Mika Ito, Eriko F. Jimbo, Chika Watanabe, Shuji Hishikawa, Takeshi Nakajima, Takanori Yamagata
Topics & Concepts
Cisterna magnaGLUT1BiologyGlucose transporterGenetic enhancementGreen fluorescent proteinMolecular biologyCerebrospinal fluidGeneEndocrinologyNeuroscienceBiochemistryInsulinMetabolism and Genetic DisordersPancreatic function and diabetesVirus-based gene therapy research