Modified cyclodextrin-based nanoparticles mediated delivery of siRNA for huntingtin gene silencing across an in vitro BBB model
Monique Culturato Padilha Mendonça, Michael F. Cronin, John F. Cryan, Caitríona M. O’Driscoll
Topics & Concepts
HuntingtinGene silencingSmall interfering RNABlood–brain barrierChemistryRNA interferenceIn vitroHuntingtin ProteinGene deliveryHuntington's diseasePharmacologyCell biologyTransfectionCancer researchBiologyCentral nervous systemNeuroscienceGeneMedicineRNABiochemistryDiseasePathologyGenetic Neurodegenerative DiseasesRNA Research and SplicingRNA Interference and Gene Delivery