Gene therapy for monogenic disorders: challenges, strategies, and perspectives

Yi Zhang, Zhi‐Ying Wu

2023Journal of genetics and genomics/Journal of Genetics and Genomics33 citationsDOI

Topics & Concepts

Genetic enhancementDiseaseMedicineImmunogenicityGene deliveryBioinformaticsGeneComputational biologyBiologyGeneticsImmunologyPathologyImmune systemCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA Interference and Gene Delivery