CRISPR/Cas-based gene editing in therapeutic strategies for beta-thalassemia
Shujun Zeng, Shuang-Yin Lei, Chao Qu, Yue Wang, Shuzhi Teng, Ping Huang
Topics & Concepts
CRISPRGenome editingBiologyThalassemiaGenetic enhancementCas9Hematopoietic stem cell transplantationTransplantationImmunologyGeneticsBioinformaticsStem cellGeneMedicineInternal medicineCRISPR and Genetic EngineeringHemoglobinopathies and Related Disorders