Specific Expression of Glial-Derived Neurotrophic Factor in Muscles as Gene Therapy Strategy for Amyotrophic Lateral Sclerosis
Guillem Mòdol‐Caballero, Belén García-Lareu, Mireia Herrando‐Grabulosa, Sergi Verdés, Rubén López‐Vales, Gemma Pagès, Miguel Chillón, Xavier Navarro, Assumpció Bosch
Topics & Concepts
Glial cell line-derived neurotrophic factorNeurotrophic factorsAmyotrophic lateral sclerosisNeuroprotectionMedicineNeuromuscular junctionNeuroscienceGDNF family of ligandsPathologyInternal medicineBiologyReceptorDiseaseAmyotrophic Lateral Sclerosis ResearchNeurogenetic and Muscular Disorders ResearchNerve injury and regeneration