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Selumetinib in the Treatment of Symptomatic Intractable Plexiform Neurofibromas in Neurofibromatosis Type 1: A Prospective Case Series with Emphasis on Side Effects

Francesco Baldo, A. Grasso, Luisa Cortellazzo Wiel, Alessandra Maestro, Marta Paulina Trojniak, Flora Maria Murru, Luca Basso, Andrea Magnolato, Irene Bruno, Egidio Barbi

2020Pediatric Drugs31 citationsDOI

Topics & Concepts

SelumetinibMedicineNeurofibromatosisAdverse effectProspective cohort studyNeurofibromaIrritabilityPediatric cancerInternal medicineSurgeryPediatricsCancerPathologyKRASColorectal cancerMenopauseNeurofibromatosis and Schwannoma CasesTuberous Sclerosis Complex ResearchSympathectomy and Hyperhidrosis Treatments
Selumetinib in the Treatment of Symptomatic Intractable Plexiform Neurofibromas in Neurofibromatosis Type 1: A Prospective Case Series with Emphasis on Side Effects | Litcius