Efficacy and safety of anti-CD45–saporin as conditioning agent for RAG deficiency
Maria Carmina Castiello, Marita Bosticardo, Nicolò Sacchetti, Enrica Calzoni, Elena Fontana, Yasuhiro Yamazaki, Elena Draghici, Cristina Corsino, Ileana Bortolomai, Lucia Piceni Sereni, Hsin‐Hui Yu, Paolo Uva, Rahul Palchaudhuri, David T. Scadden, Anna Villa, Luigi D. Notarangelo
Topics & Concepts
Recombination-activating geneImmune systemImmunodeficiencySaporinSevere combined immunodeficiencyBiologyImmunologyTotal body irradiationTransplantationBone marrowHaematopoiesisCancer researchAntibodyStem cellMonoclonal antibodyMedicineCell biologyInternal medicineImmunotoxinCyclophosphamideGeneRecombinationGeneticsChemotherapyBiochemistryImmunodeficiency and Autoimmune DisordersT-cell and B-cell ImmunologyHematopoietic Stem Cell Transplantation