Reversal of RNA toxicity in myotonic dystrophy via a decoy RNA-binding protein with high affinity for expanded CUG repeats
Ludovic Arandel, Magdalena Matłoka, Arnaud F. Klein, Frédérique Rau, Alain Sureau, Michel Ney, Aurélien Cordier, Maria Kondili, Micaela Polay-Espinoza, Naïra Naouar, Arnaud Ferry, Mégane Lemaître, Séverine Bégard, Morvane Colin, Chloé Lamarre, Hélène Tran, Luc Buée, Joëlle Marie, Nicolas Sergeant, Denis Furling
Topics & Concepts
Myotonic dystrophyDecoyRNA-binding proteinRNA splicingRNABiologyTrinucleotide repeat expansionCell biologyAlternative splicingMessenger RNAExonMutantMolecular biologyGeneGeneticsReceptorAlleleGenetic Neurodegenerative DiseasesMuscle Physiology and DisordersRNA Research and Splicing