Alternative splicing in neurodegenerative disease and the promise of RNA therapies
David Nikom, Sika Zheng
Topics & Concepts
RNA splicingAlternative splicingDiseaseAmyotrophic lateral sclerosisFrontotemporal dementiaMechanism (biology)NeuroscienceRNA-binding proteinDementiaMedicineBiologyBioinformaticsRNAGene isoformGeneGeneticsPathologyPhilosophyEpistemologyRNA Research and SplicingAmyotrophic Lateral Sclerosis ResearchNeurogenetic and Muscular Disorders Research