Inhaled delivery of a lipid nanoparticle encapsulated messenger RNA encoding a ciliary protein for the treatment of primary ciliary dyskinesia
Caroline Woo, Ayed Allawzi, Nicholas Clark, Neha Kaushal, Tim Efthymiou, Maike Thamsen, Jane Nguyen, Richard Wooster, James C. Sullivan
Topics & Concepts
Primary ciliary dyskinesiaCiliumMessenger RNAMotile ciliumCell biologyGeneBiologyMolecular biologyMedicinePathologyGeneticsInternal medicineLungBronchiectasisCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchGenetic and Kidney Cyst Diseases