Gene therapy and gene editing strategies in inherited blood disorders
Xuemei Song, JinLei Liu, Tangcong Chen, Tingfeng Zheng, Xiaolong Wang, Xiang Guo
Topics & Concepts
Genetic enhancementGenome editingGeneGeneticsComputational biologyBiologyBioinformaticsMedicineCRISPRCRISPR and Genetic EngineeringRNA regulation and diseaseVirus-based gene therapy research