Lumacaftor-ivacaftor effects on cystic fibrosis-related liver involvement in adolescents with homozygous F508 del-CFTR
David Drummond, Jérémy Dana, Laureline Berteloot, Elena K. Schneider‐Futschik, F. Chedevergne, Céline Bailly-Botuha, Thao Nguyen‐Khoa, Mathieu Cornet, Muriel Le Bourgeois, Dominique Debray, M Girard, Isabelle Sermet‐Gaudelus
Topics & Concepts
IvacaftorMedicineCystic fibrosisCystic fibrosis transmembrane conductance regulatorGastroenterologyInternal medicineLiver diseasePopulationAdverse effectEndocrinologyPathologyEnvironmental healthCystic Fibrosis Research AdvancesSinusitis and nasal conditionsGenetic and Kidney Cyst Diseases