First small-molecule drug targeting RNA gains momentum
Cormac Sheridan
Topics & Concepts
DrugRNASpinal muscular atrophySmall moleculeDrug developmentDrug discoveryComputational biologyBiologyMedicineChemistryPharmacologyBioinformaticsGeneticsGeneRNA and protein synthesis mechanismsNeurogenetic and Muscular Disorders ResearchDNA and Nucleic Acid Chemistry