Massively parallel base editing to map variant effects in human hematopoiesis
Jorge D. Martin-Rufino, Nicole Castano, Michael Pang, Emanuelle I. Grody, Samantha Joubran, Alexis Caulier, Lara Wahlster, Tongqing Li, Xiaojie Qiu, Anna Maria Riera-Escandell, Gregory A. Newby, Aziz Al’Khafaji, Santosh Kumar Chaudhary, Susan Black, Chen Weng, Glen Munson, David R. Liu, Marcin W. Włodarski, Kacie Sims, Jamie H. Oakley, Ross M. Fasano, Ramnik J. Xavier, Eric S. Lander, Daryl E. Klein, Vijay G. Sankaran
Topics & Concepts
BiologyMassively parallelHaematopoiesisBase (topology)Computational biologyGeneticsParallel computingStem cellComputer scienceMathematical analysisMathematicsCRISPR and Genetic EngineeringVirus-based gene therapy researchCytomegalovirus and herpesvirus research