CRISPR genome surgery in a novel humanized model for autosomal dominant retinitis pigmentosa
Wen-Hsuan Wu, Yi‐Ting Tsai, I‐Wen Huang, Chia-Hua Cheng, Chun‐Wei Hsu, Xuan Cui, Joseph Ryu, Peter M. J. Quinn, Salvatore Marco Caruso, Chyuan‐Sheng Lin, Stephen H. Tsang
Topics & Concepts
Retinitis pigmentosaBiologyContext (archaeology)PhenocopyHumanized mouseCRISPRGeneticsGenetic heterogeneityRhodopsinGenetic enhancementRetinal degenerationMutationGeneIn vivoRetinalPhenotypeBiochemistryPaleontologyRetinal Development and DisordersCRISPR and Genetic EngineeringAdvanced biosensing and bioanalysis techniques