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Use of Everolimus to treat cardiac rhabdomyomas and incessant arrhythmias in a newborn

Eyal Sagiv, Sathish Chikkabyrappa, Jeffrey Conwell, Mark Lewin, Terrence Un Hoong Chun

2022Annals of Pediatric Cardiology12 citationsDOIOpen Access PDF

Abstract

We report treating a term neonate with tuberous sclerosis and giant rhabdomyomas who presented with incessant supraventricular tachycardia with Everolimus. The treatment was efficient in reducing tumor size and assisted as an adjunct therapy in controlling arrhythmia and limiting preexcitation. Treatment was challenged by difficulty to achieve stable drug level and limited by neutropenia as a serious side effect.

Topics & Concepts

MedicineEverolimusTuberous sclerosisSupraventricular tachycardiaLimitingSupraventricular arrhythmiaInternal medicineTachycardiaCardiologyIntensive care medicineRadiologyAtrial fibrillationMechanical engineeringEngineeringTuberous Sclerosis Complex ResearchVascular Tumors and AngiosarcomasEosinophilic Disorders and Syndromes
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