The safety and efficacy of gene therapy treatment for monogenic retinal and optic nerve diseases: A systematic review
Alexis Ceecee Britten‐Jones, Rui Jin, Sena A. Gocuk, Elise Cichello, Fleur O’Hare, Doron G. Hickey, Thomas L. Edwards, Lauren N. Ayton
Topics & Concepts
MedicineClinical trialChoroideremiaGenetic enhancementOptic nerveOphthalmologyAchromatopsiaAdverse effectBioinformaticsRetinalInternal medicineGeneGeneticsBiologyRetinal Development and DisordersOcular Disorders and TreatmentsVirus-based gene therapy research