Targeting the population for gene therapy with MYBPC3
Lucie Carrier
Topics & Concepts
Hypertrophic cardiomyopathyMYH7MedicinePopulationAsymptomaticCardiomyopathyHeart failureSudden cardiac deathCompound heterozygositySarcomereAsymptomatic carrierGeneticsCardiologyMutationInternal medicineGeneBiologyMyocyteGene isoformEnvironmental healthCardiomyopathy and Myosin StudiesViral Infections and Immunology ResearchWilliams Syndrome Research