Economic burden of spinal muscular atrophy: an analysis of claims data
Lisa Belter, Rosángel Cruz, Sierra Kulas, Emily McGinnis, Omar Dabbous, Jill Jarecki
Abstract
: Direct costs of SMA are tremendous, often >50-fold higher compared with matched controls. Efforts are needed to reduce costs through improved standards of care.
Topics & Concepts
MedicineJuvenileSMA*Spinal muscular atrophyPediatricsNeuromuscular diseaseInternal medicineDiseaseEmergency medicineGeneticsCombinatoricsBiologyMathematicsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery