Eladocagene Exuparvovec: First Approval
Susan J. Keam
Topics & Concepts
MedicineGenetic enhancementAromatic L-amino acid decarboxylaseAdeno-associated virusPharmacotherapyClinical trialGenePharmacologyInternal medicinePediatricsVector (molecular biology)Recombinant DNAGeneticsDopamineBiologyMetabolism and Genetic DisordersAdipose Tissue and MetabolismBiotin and Related Studies