The U UGA C sequence provides a favorable context to ELX-02 induced CFTR readthrough
Iwona Pranke, Jessica Varilh, Aurélie Hatton, Caroline Faucon, Emmanuelle Girodon, Elise Dréano, B. Chevalier, Sabrina Karri, Philippe Reix, I. Durieu, Laure Bidou, Olivier Namy, Magali Taulan‐Cadars, Alexandre Hinzpeter, Isabelle Sermet‐Gaudelus
Topics & Concepts
Cystic fibrosisMedicineContext (archaeology)Sequence (biology)GeneticsComputational biologyInternal medicineBiologyPaleontologyNeonatal Respiratory Health ResearchCystic Fibrosis Research AdvancesEpigenetics and DNA Methylation