Inhaled mRNA therapy for treatment of cystic fibrosis: Interim results of a randomized, double‐blind, placebo‐controlled phase 1/2 clinical study
Steven M. Rowe, Jonathan B. Zuckerman, Daniel Dorgan, Jorge Lascano, Karen McCoy, Manu Jain, Michael S. Schechter, Sherstin T. Lommatzsch, V. Indihar, Noah Lechtzin, Kimberly McBennett, Caroline Callison, Cynthia D. Brown, Theodore G. Liou, Kelvin D. MacDonald, Samya Z. Nasr, Susan Bodie, M. Vaughn, Eric B. Meltzer, Ann Barbier
Topics & Concepts
MedicinePlaceboCohortAdverse effectCystic fibrosisDosingInternal medicineRandomized controlled trialPlacebo-controlled studyGastroenterologyAnesthesiaDouble blindPathologyAlternative medicineCystic Fibrosis Research AdvancesRNA Interference and Gene DeliveryInhalation and Respiratory Drug Delivery