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Reported Adverse Events in a Multicenter Cohort of Patients Ages 6-18 Years with Cystic Fibrosis and at Least One F508del Allele Receiving Elexacaftor/Tezacaftor/Ivacaftor

Vito Terlizzi, Cristina Fevola, Santiago Presti, Alice Castaldo, Valeria Daccò, Laura Claut, Angela Sepe, Fabio Majo, Rosaria Casciaro, Iréne Esposito, Pamela Vitullo, M Salvi, Patrizia Troiani, Francesca Ficili, Giuseppe Fabio Parisi, Stefano Pantano, Stefano Costa, Giuseppina Leonetti, Nicola Palladino, Giovanni Taccetti, Paolo Bonomi, Donatello Salvatore

2024The Journal of Pediatrics24 citationsDOI

Topics & Concepts

IvacaftorMedicineCystic fibrosisAlleleCohortAdverse effectCohort studyInternal medicinePediatricsGeneticsCystic fibrosis transmembrane conductance regulatorGeneBiologyCystic Fibrosis Research AdvancesAsthma and respiratory diseasesPediatric health and respiratory diseases
Reported Adverse Events in a Multicenter Cohort of Patients Ages 6-18 Years with Cystic Fibrosis and at Least One F508del Allele Receiving Elexacaftor/Tezacaftor/Ivacaftor | Litcius