Suppression of proteolipid protein rescues Pelizaeus–Merzbacher disease
Matthew S. Elitt, Lilianne Barbar, H. Elizabeth Shick, Berit Powers, Yuka Maeno-Hikichi, Mayur Madhavan, Kevin Allan, Baraa S. Nawash, Artur S. Gevorgyan, Stevephen Hung, Zachary S. Nevin, Hannah Olsen, Midori Hitomi, Daniela Schlatzer, Hien Zhao, Adam Swayze, David F. LePage, Weihong Jiang, Ronald A. Conlon, Frank Rigo, Paul J. Tesar
Topics & Concepts
Proteolipid protein 1LeukodystrophyPoint mutationBiologyMyelinOligodendrocyteMutationMyelin proteolipid proteinGeneticsGeneMedicineMyelin basic proteinNeuroscienceInternal medicineDiseaseCentral nervous systemRNA regulation and diseaseRNA Research and SplicingRNA modifications and cancer