Litcius/Paper detail

Molecular approaches for the treatment and prevention of Friedreich's ataxia

Wenyao Yang, Bruce Thompson, Faith Kwa

2021Drug Discovery Today10 citationsDOI

Topics & Concepts

FrataxinAtaxiaTrinucleotide repeat expansionGene silencingDiseaseBiologyBioinformaticsClinical trialGeneGeneticsMedicineNeurosciencePathologyIron-binding proteinsAlleleGenetic Neurodegenerative DiseasesMitochondrial Function and PathologyDNA Repair Mechanisms