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CRISPR/Cas9-based gene-editing technology for sickle cell disease

Liangliang Ma, Shanglun Yang, Qianya Peng, Jingping Zhang, Jing Zhang, Jing Zhang, Jing Zhang

2023Gene36 citationsDOI

Topics & Concepts

CRISPRGenome editingBiologyCas9Genetic enhancementDiseaseGeneHematopoietic stem cell transplantationComputational biologyGeneticsBioinformaticsStem cellMedicineInternal medicineCRISPR and Genetic EngineeringHemoglobinopathies and Related DisordersRNA regulation and disease
CRISPR/Cas9-based gene-editing technology for sickle cell disease | Litcius