Amelioration of an Inherited Metabolic Liver Disease through Creation of a De Novo Start Codon by Cytidine Base Editing
Lei Yang, Liren Wang, Yanan Huo, Xi Chen, Shuming Yin, Yaqiang Hu, Xiaohui Zhang, Rui Zheng, Hongquan Geng, Honghui Han, Xueyun Ma, Meizhen Liu, Haibo Li, Weishi Yu, Mingyao Liu, Jun Wang, Dali Li
Topics & Concepts
CytidineBiologyGeneticsGenome editingStop codonBase (topology)Computational biologyGeneCRISPRBiochemistryEnzymeMathematicsMathematical analysisCRISPR and Genetic EngineeringRNA and protein synthesis mechanismsGenetics and Neurodevelopmental Disorders