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Current and emerging therapies for Duchenne muscular dystrophy and spinal muscular atrophy

Mohsan Iftikhar, Justin Frey, Md.Jasimuddin Shohan, Sohail Malek, Shaker A. Mousa

2020Pharmacology & Therapeutics80 citationsDOI

Topics & Concepts

Spinal muscular atrophySMN1MedicineDuchenne muscular dystrophySMA*Neuromuscular diseaseDystrophinMuscular dystrophyWastingWeaknessBioinformaticsInternal medicineSurgeryDiseaseBiologyCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchMuscle Physiology and DisordersGenetics and Neurodevelopmental Disorders
Current and emerging therapies for Duchenne muscular dystrophy and spinal muscular atrophy | Litcius