Gene therapy for neovascular age-related macular degeneration by subretinal delivery of RGX-314: a phase 1/2a dose-escalation study
Peter A. Campochiaro, Robert L. Avery, David M. Brown, Jeffrey S. Heier, Allen C. Ho, Stephen Huddleston, Glenn J. Jaffe, Arshad M. Khanani, Stephen Pakola, Dante J. Pieramici, Charles C. Wykoff, Sherri Van Everen
Topics & Concepts
Macular degenerationMedicineChoroidal neovascularizationOphthalmologyOncologyRetinal Diseases and TreatmentsRetinal Development and DisordersVirus-based gene therapy research