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Human genetic diversity alters off-target outcomes of therapeutic gene editing

Samuele Cancellieri, Jing Zeng, Linda Yingqi Lin, Manuel Tognon, My Anh Nguyen, Jiecong Lin, Nicola Bombieri, Stacy A. Maitland, Marioara-Felicia Ciuculescu, Varun Katta, Shengdar Q. Tsai, Myriam Armant, Scot A. Wolfe, Rosalba Giugno, Daniel E. Bauer, Luca Pinello

2022Nature Genetics111 citationsDOIOpen Access PDF

Topics & Concepts

BiologyGenome editingGenetic diversityGeneComputational biologyDiversity (politics)GeneticsHuman genetic variationEvolutionary biologyCRISPRHuman genomeGenomePopulationDemographyAnthropologySociologyCRISPR and Genetic EngineeringInnovation and Socioeconomic DevelopmentViral Infections and Immunology Research
Human genetic diversity alters off-target outcomes of therapeutic gene editing | Litcius