CRISPR/Cas9 System as a Promising Therapy in Thalassemia and Sickle Cell Disease: A Systematic Review of Clinical Trials
Rehab Ahmed, Wafa N. Alghamdi, Fahad A. Al‐Harbi, Huda D. Alatawi, Kawthar M. Alenezi, Turki F. Alanazi, Nehal M. Elsherbiny
Topics & Concepts
CRISPRFetal hemoglobinGenetic enhancementGenome editingDiseaseThalassemiaCas9MedicineClinical trialBiologyBioinformaticsGeneticsGeneInternal medicinePregnancyFetusCRISPR and Genetic EngineeringHemoglobinopathies and Related DisordersEvolution and Genetic Dynamics