Serum extracellular vesicles for delivery of CRISPR-CAS9 ribonucleoproteins to modify the dystrophin gene
Nathalie Majeau, Annabelle Fortin-Archambault, Catherine Gérard, Joël Rousseau, Pouiré Yaméogo, Jacques P. Tremblay
Topics & Concepts
RibonucleoproteinCRISPRDuchenne muscular dystrophyBiologyCas9DystrophinGuide RNACell biologyExonMicrovesiclesMolecular biologyExosomeIntronGeneRNAGeneticsmicroRNAExtracellular vesicles in diseaseRNA Interference and Gene DeliveryRNA Research and Splicing