Update of treatment for Gaucher disease
Weijing Kong, Cheng Lu, Yingxue Ding, Yan Meng
Topics & Concepts
MedicineDiseaseIntensive care medicineLysosomal storage disordersSubstrate reduction therapyOrphan drugPediatricsBioinformaticsPathologyEnzyme replacement therapyBiologyLysosomal Storage Disorders ResearchCellular transport and secretionCalcium signaling and nucleotide metabolism