A de novo YY1 missense variant expanding the Gabriele-de Vries syndrome phenotype and affecting X-chromosome inactivation
Suely Rodrigues dos Santos, Rafael Mina Piergiorge, J.M.A.M. Rocha, Bianca Barbosa Abdala, Andressa Pereira Gonçalves, Márcia Mattos Gonçalves Pimentel, Cíntia Barros Santos-Rebouças
Topics & Concepts
HaploinsufficiencyMissense mutationYY1GeneticsBiologyX-inactivationPhenotypeGeneX chromosomePromoterGene expressionGenomic variations and chromosomal abnormalitiesGenomics and Rare DiseasesGenetics and Neurodevelopmental Disorders