Emicizumab prophylaxis in patients with acquired haemophilia A (GTH-AHA-EMI): an open-label, single-arm, multicentre, phase 2 study
Andreas Tiede, Christina Hart, Paul Knöbl, Richard Greil, Johannes Oldenburg, Ulrich J. Sachs, Wolfgang Miesbach, Christian Pfrepper, Karolin Trautmann‐Grill, Katharina Holstein, Ján Pilch, Patrick Möhnle, Christoph Schindler, Carmen Weigt, Dorothea Schipp, Marcus May, Christiane Dobbelstein, Fabius J. Pelzer, Sonja Werwitzke, Robert Klamroth
Topics & Concepts
MedicineHaemophiliaImmunosuppressionHaemophilia AInternal medicineClinical endpointAdverse effectPopulationSurgeryClinical trialPediatricsEnvironmental healthHemophilia Treatment and ResearchBlood transfusion and managementProtein purification and stability