Gain and loss of abilities in type II SMA: A 12-month natural history study
Giorgia Coratti, Simona Lucibello, Maria Carmela Pera, Tina Duong, R. Muni Lofra, Matthew Civitello, Adele D’Amico, Nathalie Goemans, Basil T. Darras, Claudio Bruno, Valeria Sansone, John Day, A. Nascimento Osorio, Francesco Muntoni, Jaccqueline Montes, Maria Sframeli, Richard S. Finkel, Eugenio Mercuri
Topics & Concepts
SMA*Natural historyNatural (archaeology)PsychologyHistoryMedicineComputer scienceInternal medicineArchaeologyAlgorithmNeurogenetic and Muscular Disorders ResearchCardiac Structural Anomalies and RepairGenetics and Neurodevelopmental Disorders