Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio
Megan A. Waldrop, Shannon Chagat, Michael A. Storey, Alayne P. Meyer, M. Iammarino, Natalie F. Reash, Lindsay N. Alfano, Linda Lowes, Garey Noritz, Andre Prochoroff, Ian Rossman, Matthew L. Ginsberg, Kathryn Mosher, Eileen Broomall, Nancy Bass, Courtney Gushue, Kavitha Kotha, Grace Paul, Richard Shell, Chang‐Yong Tsao, Jerry R. Mendell, Anne M. Connolly
Topics & Concepts
MedicineSMA*Adverse effectSpinal muscular atrophyCohortSMN1PediatricsDiseaseInternal medicineCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCRISPR and Genetic Engineering