Litcius/Paper detail

Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio

Megan A. Waldrop, Shannon Chagat, Michael A. Storey, Alayne P. Meyer, M. Iammarino, Natalie F. Reash, Lindsay N. Alfano, Linda Lowes, Garey Noritz, Andre Prochoroff, Ian Rossman, Matthew L. Ginsberg, Kathryn Mosher, Eileen Broomall, Nancy Bass, Courtney Gushue, Kavitha Kotha, Grace Paul, Richard Shell, Chang‐Yong Tsao, Jerry R. Mendell, Anne M. Connolly

2023Neuromuscular Disorders23 citationsDOI

Topics & Concepts

MedicineSMA*Adverse effectSpinal muscular atrophyCohortSMN1PediatricsDiseaseInternal medicineCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCRISPR and Genetic Engineering
Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio | Litcius