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Complement activation in a phase Ib study of fordadistrogene movaparvovec for Duchenne muscular dystrophy

Barry J. Byrne, Russell J. Butterfield, Perry B. Shieh, Edward C. Smith, Christoph Licht, Michael Binks, Sandra Casinghino, Marielle Delnomdedieu, Kodihalli C. Ravindra, T Mcdonnell, Kelly A. Ryan, Martin Schulz, Qi Shen, Heliang Shi, Madhu P. Sirivelu, Vishal S. Vaidya, Laurence O. Whiteley, David Lévy

2025Molecular Therapy11 citationsDOIOpen Access PDF

Topics & Concepts

Duchenne muscular dystrophyComplement systemComplement (music)Muscular dystrophyAlternative complement pathwayBiologyImmunologyMedicineCell biologyGeneticsAntibodyGenePhenotypeComplementationMuscle Physiology and DisordersAdenosine and Purinergic SignalingCardiac Fibrosis and Remodeling
Complement activation in a phase Ib study of fordadistrogene movaparvovec for Duchenne muscular dystrophy | Litcius