The Promise of PCSK9 and Lipoprotein(a) as Targets for Gene Silencing Therapies
Dick C. Chan, Gerald F. Watts
Topics & Concepts
PCSK9MedicineGene silencingKexinProprotein convertaseSmall interfering RNADyslipidemiaLipoprotein(a)Clinical trialFamilial hypercholesterolemiaRNA interferenceDiseaseLDL receptorLipoproteinInternal medicinePharmacologyCancer researchBioinformaticsCholesterolGeneRNABiologyGeneticsLipoproteins and Cardiovascular HealthAtherosclerosis and Cardiovascular DiseasesCholesterol and Lipid Metabolism