Litcius/Paper detail

Valoctocogene Roxaparvovec: First Approval

Hannah A. Blair

2022Drugs85 citationsDOIOpen Access PDF

Topics & Concepts

MedicineHaemophiliaMarketing authorizationAuthorizationPharmacotherapyHaemophilia AVirologyPediatricsAdeno-associated virusInternal medicineBioinformaticsGeneRecombinant DNAVector (molecular biology)GeneticsComputer scienceComputer securityBiologyHemophilia Treatment and ResearchCancer-related gene regulation