Precision modeling of mitochondrial disease in rats via DdCBE-mediated mtDNA editing
Xiaolong Qi, Xiaoxu Chen, Jiayin Guo, Xu Zhang, Haifeng Sun, Jianying Wang, Xuezhen Qian, Bo Li, Lei Tan, Lei Yu, Wei Chen, Lianfeng Zhang, Yuanwu Ma, Bin Shen
Topics & Concepts
Mitochondrial DNAMitochondrial diseaseBiologyGenome editingComputational biologyMitochondrionGeneticsCRISPRGeneMitochondrial Function and PathologyMetabolism and Genetic DisordersAmino Acid Enzymes and Metabolism