Facioscapulohumeral muscular dystrophy: the road to targeted therapies
Mara S. Tihaya, Karlien Mul, Judit Balog, Jessica C. de Greef, Stephen J. Tapscott, Rabi Tawil, Jeffrey Statland, Silvère M. van der Maarel
Topics & Concepts
Facioscapulohumeral muscular dystrophyMedicineEpigeneticsClinical trialDiseaseMuscular dystrophyBioinformaticsMechanism (biology)GeneticsGeneInternal medicineBiologyEpistemologyPhilosophyMuscle Physiology and DisordersCardiomyopathy and Myosin StudiesCRISPR and Genetic Engineering