Monitoring of asymptomatic family members at risk of hereditary transthyretin amyloidosis for early intervention with disease-modifying therapies
Mitsuharu Ueda, Yoshiki Sekijima, Haruki Koike, Taro Yamashita, Tsuneaki Yoshinaga, Tomonori Ishii, Yukio Ando
Topics & Concepts
MedicineAsymptomaticTransthyretinDiseaseAmyloidosisIntervention (counseling)Asymptomatic carrierIntensive care medicinePediatricsInternal medicinePsychiatryAmyloidosis: Diagnosis, Treatment, OutcomesAlzheimer's disease research and treatmentsDermatological and Skeletal Disorders