Litcius/Paper detail

Efficient mitochondrial A-to-G base editors for the generation of mitochondrial disease models

Liang Chen, Mengjia Hong, Changming Luan, Meng Yuan, Yiming Wang, Xinyuan Guo, Yue Fang, Hao Huang, Xiaohua Dong, Hongyi Gao, Dan Zhang, Xi Chen, Dong Meng, Molin Huang, Zongyi Yi, Mingyao Liu, Wensheng Wei, Liangcai Gao, Gaojie Song, Xiaoming Zhou, Dali Li

2025Nature Biotechnology15 citationsDOI

Topics & Concepts

Mitochondrial DNAMitochondrial diseaseMitochondrionBase (topology)BiologyComputational biologyChemistryCell biologyGeneticsGeneMathematicsMathematical analysisCRISPR and Genetic EngineeringMitochondrial Function and PathologyGenetics, Aging, and Longevity in Model Organisms