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Early treatment is a lifeline for infants with SMA

Charlotte J. Sumner, Thomas O. Crawford

2022Nature Medicine19 citationsDOIOpen Access PDF

Topics & Concepts

Spinal muscular atrophySMA*MedicinePediatricsIntensive care medicineComputer scienceAlgorithmNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery
Early treatment is a lifeline for infants with SMA | Litcius