O19 Preliminary results from MLB-01-003: an open label phase 2 study of BBP-418 in patients with limb-girdle muscular dystrophy type 2I/R9
A. Harper, R. Langeslay, T. Rajasingham, H. Rodriguez, T. Blankenbiller, A. Hutchaleelaha, D. Sproule
Topics & Concepts
Limb-girdle muscular dystrophyMedicineMuscular dystrophyPhysical medicine and rehabilitationInternal medicineChemistryBiochemistryMutationGeneMuscle Physiology and DisordersNeurogenetic and Muscular Disorders ResearchGenetic Neurodegenerative Diseases